Young children with Duchenne muscular dystrophy can now get the first gene therapy promising to treat the crippling and fatal muscle condition. But it is expected to cost millions of dollars.
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The drug, from Sarepta Therapeutics, promises to repair the defective gene at the root of the fatal disorderThe Food and Drug Administration approved the therapy for Duchenne muscular dystrophy, following a fast-track review.Young children with Duchenne muscular dystrophy can now get the first gene therapy for the crippling muscle condition.Continue reading your article with
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